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News and Treatment Updates

Here's where you'll find a regularly updated, broad range of articles written by the AAMDSIF team, allied health organizations and news organizations. By staying well-informed, patients and families are practicing a form of self-support that will help them be more effective self-advocates when engaging with health care providers.

ASH 2021 Recap: Multi Omics Sheds New Light on Malignant Transformation from Myeloproliferative Neoplasm to AML

Originally Published: 12/21/2021
Article Source: External Web Content
Link above leads to podcast recording. 

Monitoring Amphiregulin May Be Warranted in Caring for Patients with Acute GVHD

Originally Published: 12/19/2021
Article Source: External Web Content
Amphiregulin (AREG) may represent a useful longitudinal monitoring biomarker for patients with life-threatening acute graft-vs-host disease (GVHD), according to a sample of 2 prospective clinical trials that was presented at the 2021 ASH Annual Meeting. Specifically, patients with a high baseline of AREG are at an increased mortality risk and, therefore, should be monitored consistently during serial assessments. Specifically, in a multivariate analysis for survival, day 28 responses (risk ratio [RR], 9.14; P <.0001) and baseline AREG (>212 pg/mL; RR, 2.72; P <.05) were the only...

Women With AML Have Worse Outcomes With Gemtuzumab Ozogamicin

Originally Published: 12/17/2021
Article Source: External Web Content
Combination gemtuzumab ozogamicin (GO) and cytarabine is no more effective than standard chemotherapy for older adults with previously untreated, standard-risk acute myeloid leukemia (AML), a phase 2/3 trial suggests.  In fact, GO plus cytarabine was associated with worse event-free survival (EFS) in women.  These findings were presented at the 2021 American Society of Hematology (ASH) Annual Meeting by Juliette Lambert, MD, PhD, of Versailles Hospital in France.  (Article continues at link.)

Aspaveli® (pegcetacoplan) approved in EU as orphan drug for treatment of PNH

Originally Published: 12/15/2021
Article Source: External Web Content
Published: Dec 15, 2021       STOCKHOLM, Dec. 15, 2021 /PRNewswire/ -- The first targeted C3 therapy approved in the EU Approval based on results from head-to-head PEGASUS phase 3 study where Aspaveli demonstrated superiority to eculizumab in improving haemoglobin levels1 Aspaveli will have market exclusivity for paroxysmal nocturnal haemoglobinuria (PNH) based on orphan drug designation Swedish Orphan Biovitrum AB (publ) (Sobi™) (STO:SOBI) and Apellis Pharmaceuticals Inc   (Nasdaq: APLS) announced today that the European Commission (EC) has approved Aspaveli® (pegcetacoplan), the first and...

FDA Approves First Drug to Prevent Graft Versus Host Disease

Originally Published: 12/15/2021
Article Source: External Web Content
Today, the U.S. Food and Drug Administration approved Orencia (abatacept) for the prophylaxis (prevention) of acute graft versus host disease (aGVHD), a condition that occurs when donor bone marrow or stem cells attack the graft recipient, in combination with certain immunosuppressants. Orencia may be used in adults and pediatric patients two years of age or older undergoing hematopoietic stem cell transplantation (commonly known as bone marrow transplantation or stem cell transplantation) from an unrelated donor.  This is the first FDA drug approval for aGVHD prevention and incorporates...

Certain Patients With Myelodysplastic Syndromes, Acute Leukemia at Higher Risk of Severe COVID-19 Illness

Originally Published: 12/14/2021
Article Source: External Web Content
Myelodysplastic syndromes (MDS) and neutropenia were both found to be strong, independent predictors of severe COVID-19 illness in patients with acute leukemia or MDS who developed COVID-19, according to data from the American Society of Hematology (ASH) RC COVID-19 Registry for Hematology presented at the ASH Annual Meeting and Exposition 2021. However, active disease alone for hospitalized patients was not associated with greater odds of dying from COVID-19, nor was receiving ongoing cancer treatment, according to the study. The analysis included data from 135 patients with acute myeloid...

Coronavirus (COVID-19) Update: FDA Authorizes New Long-Acting Monoclonal Antibodies for Pre-exposure Prevention of COVID-19 in Certain Individuals

Originally Published: 12/08/2021
Article Source: External Web Content
Today, the U.S. Food and Drug Administration issued an emergency use authorization (EUA) for AstraZeneca’s Evusheld (tixagevimab co-packaged with cilgavimab and administered together) for the pre-exposure prophylaxis (prevention) of COVID-19 in certain adults and pediatric individuals (12 years of age and older weighing at least 40 kilograms [about 88 pounds]).  The product is only authorized for those individuals who are not currently infected with the SARS-CoV-2 virus and who have not recently been exposed to an individual infected with SARS-CoV-2. The authorization also requires that...

mRNA COVID-19 Vaccination Sparks Strong Antibody Response in Patients With AML and MDS

Originally Published: 11/30/2021
Article Source: External Web Content
The mRNA COVID-19 Vaccines Are Safe and Effective for Most Patients with Cancer For most patients with cancer, the mRNA COVID-19 vaccines are safe and effective. This article explains the results of the first study that evaluated the safety and effectiveness of the mRNA vaccines in patients with solid cancers, such as lung, breast, or prostate cancer. November 2021 – Lung Cancer Laura Morgan The recent death of Colin L. Powell in October 2021 from COVID-19 complications led to a flurry of questions and misinformation. Although he received 2 shots of an mRNA vaccine, people ignored the...

FDA Approves First Treatment for Common Type of Post-Transplant Infection that is Resistant to Other Drugs

Originally Published: 11/23/2021
Article Source: External Web Content
For Immediate Release: November 23, 2021   Today, the U.S. Food and Drug Administration approved Livtencity (maribavir) as the first drug for treating adults and pediatric patients (12 years of age and older and weighing at least 35 kilograms) with post-transplant cytomegalovirus (CMV) infection/disease that does not respond (with or without genetic mutations that cause resistance) to available antiviral treatment for CMV. Livtencity works by preventing the activity of human cytomegalovirus enzyme pUL97, thus blocking virus replication. (Please follow the link to the complete article.)

Cost-effectiveness analysis of oral azacitidine maintenance therapy in acute myeloid leukemia

Originally Published: 11/18/2021
Article Source: External Web Content
TO THE EDITOR: Maintenance therapy in acute myeloid leukemia (AML) after induction and consolidation chemotherapy has been studied for more than 2 decades.1  No randomized trial had shown an overall survival (OS) benefit compared with observation until the recent QUAZAR AML-001 trial of oral azacitidine.2  The QUAZAR AML-001 trial randomized 472 patients with transplant-ineligible AML ≥ 55 years of age, who were in complete remission (CR) or CR with incomplete count recovery after induction and/or consolidation therapy, to maintenance therapy with oral azacitidine or placebo.2  Oral...