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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Current landscape of paroxysmal nocturnal hemoglobinuria in the era of complement inhibitors and regulators Dec 2024 Therapeutic Advances in Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pegcetacoplan: the first and only C3-targeted therapy for the treatment of adults with paroxysmal nocturnal hemoglobinuria Dec 2024 Expert Review of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Real-World Study of the Burden of Myelodysplastic Syndromes in Patients and Their Caregivers in Europe and the United States Dec 2024 Oncology and Therapy Myelodysplastic Syndromes (MDS)
Efficacy and Safety of Venetoclax Plus Azacitidine for Patients With Treatment-Naive High-Risk Myelodysplastic Syndromes Dec 2024 Blood Myelodysplastic Syndromes (MDS)
RNA splicing as a therapeutic target in myelodysplastic syndromes Dec 2024 Seminars in Hematology Myelodysplastic Syndromes (MDS)
Crovalimab in the paroxysmal nocturnal hemoglobinuria treatment landscape Dec 2024 Immunotherapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Targeted therapies for myelodysplastic syndromes/neoplasms (MDS): current landscape and future directions Nov 2024 Expert Review of Anticancer Therapy Myelodysplastic Syndromes (MDS)
Terminal complement inhibition and control of hemolysis in patients with paroxysmal nocturnal hemoglobinuria who switched from high-dose eculizumab to ravulizumab: a phase IV, single-arm clinical trial Nov 2024 Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Supportive care strategies in myelodysplastic syndromes and acute myeloid leukemia in older adults: a national survey of Canadian hematologists Nov 2024 Annals of Hematology Myelodysplastic Syndromes (MDS)
Health-related quality of life and symptom-specific functional impairment among patients treated with parenterally administered complement inhibitors for paroxysmal nocturnal hemoglobinuria Nov 2024 Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)