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A Journey from Blood Cells to Genes and Back |
Aug 2023 |
Annual Review of Genomics and Human Genetics |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria |
Aug 2023 |
Haematologica |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Factor B inhibitor iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria |
Jul 2023 |
Blood Reviews |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Efficacy and safety of the C5 inhibitor crovalimab in complement inhibitor-naive patients with PNH (COMMODORE 3): A multicenter, Phase 3, single-arm study |
Jul 2023 |
American Journal of Hematology |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Are we ready to ring in a new upfront therapy in lower-risk myelodysplastic syndromes? |
Jul 2023 |
Lancet |
Myelodysplastic Syndromes (MDS) |
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Transplantation Referral Patterns for Patients with Newly Diagnosed Higher-Risk Myelodysplastic Syndromes and Acute Myeloid Leukemia at Academic and Community Sites in the Connect® Myeloid Disease Registry: Potential Barriers to Care |
Jul 2023 |
Transplantation and Cellular Therapy |
Myelodysplastic Syndromes (MDS) |
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Efficacy and safety of luspatercept versus epoetin alfa in erythropoiesis-stimulating agent-naive, transfusion-dependent, lower-risk myelodysplastic syndromes (COMMANDS): interim analysis of a phase 3, open-label, randomised controlled trial |
Jul 2023 |
Lancet |
Myelodysplastic Syndromes (MDS) |
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Health-related quality of life and vulnerability among people with myelodysplastic syndromes: a US national study |
Jul 2023 |
Blood Advances |
Myelodysplastic Syndromes (MDS) |
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Activity of luspatercept and ESAs combination for treatment of anemia in lower-risk myelodysplastic syndromes |
Jul 2023 |
Blood Advances |
Myelodysplastic Syndromes (MDS) |
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Novel targeted C3 inhibitor pegcetacoplan for paroxysmal nocturnal hemoglobinuria |
Jul 2023 |
Clinical and Experimental Medicine |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
